Repurposing drugs for treating the neurobehavioral manifestations of PTEN hamartoma tumor syndrome

Authors: Tim Fieblinger, Judith Rudolph, Kerstin Müller, Petra Friess, Nicole Weigelt, Christina Thiede, Simone Modolo, Denise Federico, Malik Majandinow, Federico Tinarelli, Vivian J.A. Costantini, Pier P. Marrese, Annalisa Mercuri, Nikisha Carty, Ana Christina Gomes, Maria A. Whitehead, Philip A. Gerrard, Chrisovalantis Papadopoulos, and Paul Elvin

iScience, 17 April 2026